Attend

Facilitate Live is again proud to present our Orphan Drugs and Rare Diseases Global Congress 2024 Americas. It’s the 22nd in the series of our Flagship tri-annual Orphan Drugs & Rare Diseases event. This congress will provide you with a comprehensive overview of the critical issues shaping the future of Orphan Drugs.

In the United States, 1 in 10 people, or around 30 million Americans are affected by more than 10,000 known rare diseases. Rare disease are classified as any disease which affects less than 200,000 Americans. Most rare diseases are life threatening and many does not have treatment. Half of the sufferers are children and 30 percent of them will die before the age of 5, due to lack of available treatment. The complex biology and lack of understanding of the natural history of rare diseases makes drug, biologic, and device development in rare diseases very challenging.

Accurate diagnosis and treatment for these diseases has also been teeming with regulatory and logistical barriers. There is an urgent need for a regulatory framework that encourages safe therapeutic innovations and helps ensure their timely access to patients.

According to reports (Fortune Business Insights), the global Orphan Drugs Market size is projected to reach USD 368.43 billion in 2030, at a CAGR of 11.6% during the forecast period, 2023-2030. Biological Orphan drug which has been use in treating rare diseases and in oncology therapy area possesses a substantially higher share in the global market as new cancer-related disease emerges and series of FDA approvals will result in increased commercialization of these drugs. The growing demand for immunomodulators will also contribute to the orphan drugs market growth. Increasing R&D initiatives and investments by prominent players and patient advocacy involvement have resulted in major pharmaceutical breakthroughs, and the development of blockbuster drugs for the treatment of several rare diseases will create opportunities and contribute exponentially to the overall market growth.

The two-day Congress will provide an interactive, cutting edge, and comprehensive discussion and networking format led by key experts with intimate knowledge in the industry. Gain practical strategies and best practices on challenges, innovations, technologies, and concepts surrounding orphan drugs and rare diseases.

We look forward to meeting you at the Congress!