20th Orphan Drugs and Rare Diseases Global Congress 2023 Americas
Addressing Scientific and Regulatory Challenges to Advance New Treatments for Rare Diseases
Thursday 16th - Friday 17th November 2023
COMING SOON! 50 + KEY INDUSTRY EXPERT SPEAKERS
- Sanjeev Luther, President & CEO, Cornerstone Pharmaceuticals
- Caroline Kurtz, Chief Development Officer, Synlogic
- Giacomo Chiesi, Head of Global Rare Diseases, Chiesi
- Stuart Siedman, Global Head Patient Advocacy, Rare Diseases, Chiesi
- Nigel Nicholls, General Manager Northern European Cluster, Egetis Therapeutics AB
- Joslyn Crowe, Vice President, International Niemann-Pick Disease Alliance (INPDA)
- Tricha Shivas, Chief Strategy Officer, Foundation for Sarcoidosis Research
- Siddharth Jain, Medical Director –LSDs & HAE, Global Medical Affairs, Takeda
- Amit Rakhit, MD, Chief Executive Officer, Flare Therapeutics
- Mohamed H. Ladha, President & GM, North America, RECORDATI RARE DISEASES
- Rogerio Vivaldi, President, CEO, Sigilon Therapeutics, an Eli Lilly and Company
- David Young, President, Research & Development, Processa Pharmaceuticals, Inc.
- Tara J. Britt, Founder and President, Rare Disease Innovations Institute, Inc.
- Michael Eging, Founder, Executive Director, Rare Access Action Project (RAAP)
- Kelsey Carreon, Patient Engagement, Rare Access Action Project (RAAP)*
- Kristin Smedley, President, Curing Retinal Blindness Foundation
- Smitha Jagadish, Vice President, Head of Rare Diseases and New Modalities, BIAL
- Monique Mulkern, Head of Global Launch Excellence, Alexion, AstraZeneca Rare Disease
- David Ross, Patient Advocate, Rare Disease Mental Health
- Monica L Weldon, President/CEO/Founder, SYNGAP1 Foundation
- Samuel L. Seward, Jr. MD, Professor and Chair, Department of Medicine, Mount Sinai
- Jennifer McNary, Founder, One Rare
- Frank Rivera, Co-Founder/President, Stronger Than Sarcoidosis
- Andrew Leger, Head of US Business Development, Ferrer
- Craig Martin, President, Chief Engagement Officer, Rithm Health
- Eugean Jiwanmall, Sr Research Analyst, Independence Blue Cross
- Emily M. Parks, Founder, CEO, POP!
- Patricia Weltin, CEO/Founder, Beyond the Diagnosis
- Jeremy Griffin, Executive Director, New York City Hemophilia Chapter
- Senior Representative, CureDuchenne
- Jayson Slotnik, Principal and Founding Partner, Health Policy Strategies
- Shane Hegarty, Chief Scientific Officer & Co-Founder, AXONIS Therapeutics, Inc.
- Julie Yu, Chief Program Officer, Amicus Therapeutics
- Samantha K. Zappia, VP, Regulatory Affairs & Quality, Vigil Neuroscience, Inc.
- Julie Breneiser, Executive Director, Gorlin Syndrome Alliance
- Annette Maughan, CEO/Co-Founder, KBG Foundation
- Jodi M. Wolff, Vice President, Patient Advocacy & Engagement, Rejuvenate Bio

Rogerio Vivaldi
President, CEO

Caroline Kurtz
Chief Development Officer

Siddhart Jain
Medical Director, Global Medical Lead

Andrea C. Furia-Helms, M.P.H.
Director, Patient Affairs Staff, Office of Clinical Policy and Programs, Office of the Commissioner, U.S. Food and Drug Administration
U.S. Food and Drug Administration

Andrea C. Furia-Helms, M.P.H.
Director, Patient Affairs Staff, Office of Clinical Policy and Programs, Office of the Commissioner, U.S. Food and Drug Administration

Christine Von Raesfeld
Founder & CEO, People with Empathy

Nigel Nicholls
General Manager Northern European Cluster

Tricha Shivas, MBe
Chief Strategy Officer

Joslyn Crowe, MSW, MA
Vice President

Monica L Weldon
President/CEO/Founder Bridge the Gap - SYNGAP Education and Research Foundation
Bridge the Gap - SYNGAP Education and Research Foundation

Monica L Weldon
President/CEO/Founder Bridge the Gap - SYNGAP Education and Research Foundation

Giacomo Chiesi
Head of Chiesi Global Rare Diseases

Stuart Siedman
Head of Patient Advocacy

Craig Martin
CEO, Global Genes

Frank Rivera
Co-Founder/President- Stronger Than Sarcoidosis

Sanjeev Luther
President, CEO & Chairman of the Board, Cornerstone Pharmaceuticals
Cornerstone Pharmaceuticals

Sanjeev Luther
President, CEO & Chairman of the Board, Cornerstone Pharmaceuticals

Michael Eging
Founder, Executive Director

Jayson Slotnik
Principal and Founding Partner

Shane Hegarty
Chief Scientific Officer & Co-Founder

Tara J. Britt
Founder and President, Rare Disease Innovations Institute, Inc.
Rare Disease Innovations Institute, Inc.

Tara J. Britt
Founder and President, Rare Disease Innovations Institute, Inc.

Julie Yu
Chief Program Officer

David Young
President, Research & Development

Jennifer McNary
Exec. Director, Head, Patient Advocacy & Engagement, Fulcrum Therapeutics
Fulcrum Therapeutics

Jennifer McNary
Exec. Director, Head, Patient Advocacy & Engagement, Fulcrum Therapeutics

Annette Maughan
CEO/Co-Founder

Monique Mulkern
Head of Global Launch Excellence

Jeremy Griffin
Executive Director, New York City Hemophilia Chapter
New York City Hemophilia Chapter

Jeremy Griffin
Executive Director, New York City Hemophilia Chapter

Andrew Leger
Head of US Business Development

Shane Hegarty
Chief Scientific Officer & Co-Founder, AXONIS Therapeutics, Inc
AXONIS Therapeutics, Inc

Shane Hegarty
Chief Scientific Officer & Co-Founder, AXONIS Therapeutics, Inc

Patricia Weltin
CEO and Founder of the Beyond the Diagnosis

Samuel L. Seward, Jr. MD
Professor and Chair, Department of Medicine

Eugean Jiwanmall
Senior Research Analyst for Medical Policy & Technology Evaluation, Independence Blue Cross
Independence Blue Cross

Eugean Jiwanmall
Senior Research Analyst for Medical Policy & Technology Evaluation, Independence Blue Cross

Kristin Smedley
President, Curing Retinal Blindness Foundation

Smitha Jagadish
Vice President, Head of Rare Diseases and New Modalities